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Glycogen storage disease type II
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#	Item
11	Stakeholder meeting outcome statement Alglucosidase alfa (Myozyme®) for the treatment of Late-Onset Pompe Disease A stakeholder meeting was held on 9 October 2014 to discuss the development of eligibility guidelines for Add to Reading List Source URL: www.pbs.gov.au Language: English - Date: 2015-03-12 23:53:04 Lysosomal storage diseases Glycogen storage disease type II Hepatology Alglucosidase alfa Medicine Health Rare diseases
12	Case Story[removed]other name-AU1 Add to Reading List Source URL: www.gmhba.com.au Language: English - Date: 2015-01-07 22:42:04 Rheumatology Arthritis Connective tissue diseases Rheumatoid arthritis Pharmaceutical drug Myotonic dystrophy Glycogen storage disease type II Health Medicine Anatomy
13	THE SECRETARY OF HEALTH AND HUMAN SERVICES WASHINGTON, D.C[removed]MAR[removed]Joseph A. Bocchini, Jr., MD Add to Reading List Source URL: blog.rarediseases.org Language: English - Date: 2015-03-10 10:16:57 Prevention Glycogen storage disease type II Hepatology Newborn screening Screening Health Medicine Rare diseases
14	United States Pompe Community Update - October 17, 2014 Genzyme would like to share with you an important update regarding the recent United States (U.S.) Food and Drug Administration’s (FDA) approval of an expanded la Add to Reading List Source URL: www.unitedpompe.com Language: English - Date: 2014-10-20 09:46:41 Glycogen storage disease type II Hepatology Alglucosidase alfa Genzyme Anaphylaxis Allergy William Canfield Medicine Health Respiratory diseases
15	You are cordially invited to attend the 4th Annual Pompe Social & Patient Meeting Hosted by the Add to Reading List Source URL: www.unitedpompe.com Language: English - Date: 2015-03-08 21:59:05 Medicine North Carolina Glycogen storage disease type II Hepatology Duke University Durham North Carolina Health Rare diseases Lysosomal storage diseases
16	Genzyme Receives Label Expansion for Lumizyme® (alglucosidase alfa) in the United States for the treatment of Pompe Disease Add to Reading List Source URL: www.unitedpompe.com Language: English - Date: 2014-09-18 20:12:24 Glycogen storage disease type II Genzyme Medicine Health Alglucosidase alfa
17	United States Pompe Community Update, August 1, 2014 Genzyme is pleased to provide an update to the Pompe Community regarding the recent United States (U.S.) Food and Drug Administration’s (FDA) approval of an expande Add to Reading List Source URL: www.unitedpompe.com Language: English - Date: 2014-09-18 20:12:25 Hepatology Alglucosidase alfa Genzyme Anaphylaxis William Canfield Medicine Health Glycogen storage disease type II
18	THE HON SUSSAN LEY MP Minister for Health Minister for Sport MEDIA RELEASE 17 February 2015 Life-saving drug for young Pompe patients Add to Reading List Source URL: www.health.gov.au Language: English - Date: 2015-02-16 19:45:28 Rare diseases Glycogen storage disease type II Hepatology Alglucosidase alfa Genzyme Methadone William Canfield Medicine Health Lysosomal storage diseases
19	Proposed Text of The Labeling of The Drug Add to Reading List Source URL: www.lumizyme.com Language: English - Date: 2014-08-01 14:10:14 Glycogen storage disease type II Hepatology Alglucosidase alfa Hypersensitivity Anaphylaxis Medicine Health Allergology
20	ICORD[removed]Business Models for Orphan Drugs Add to Reading List Source URL: icord.se Language: English - Date: 2010-10-29 09:35:02 Drug discovery Lipid storage disorders Pharmacology Pharmaceutical industry Lysosomal storage disease Mucopolysaccharidosis Niemann–Pick disease Orphan drug Glycogen storage disease type II Health Rare diseases Medicine

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